The liposomes are designed to be absorbed by the cells lining the airways of cystic fibrosis patients, where the gene stimulates the production of the healthy protein in the cell membranes that prevents the the lungs from clogging with sticky mucus.
Screening of newborns for cystic fibrosis is now performed in every state in the United States.
As a result, the condition can be diagnosed within the first month of life, before symptoms develop.
Cystic fibrosis is caused by a faulty gene that a child inherits from both their parents.
The faulty gene affects the movement of salt and water in and out of cells.
A glimmer of hope for the thousands of families affected by cystic fibrosis has emerged from a clinical trial showing that gene therapy produced a modest but significant improvement among children suffering from the most common inherited disease of white Europeans.